Development of an academic disease registry for spinal muscular atrophy
Authors: Eugenio Mercuri, Richard S. Finkel, Mariacristina Scoto, Susan A. Hall, Susan Eaton, Aisha Rashid, Julia Balashkina, Giorgia Coratti, Maria Carmela Pera, Salma Samsuddin, Matthew Civitello, Francesco Muntoni, Darryl C. De Vivo, Basil T. Darras, John Day, Jacqueline Montes, Allan Glanzmann, Amy Pasternack, Rachel Salazar, Sally Dunaway Young, Tina Duong, Marika Pane, Beatrice Berti, Concetta Palermo, Daniela Leone, Annalia Frongia, Laura Antonaci, Roberto De Sanctis, Sonia Messina, Enrico Bertini, Giuseppe Vita, Claudio Bruno, Maria Sframeli, Valeria Sansone, Emilio Albamonte, Adele D’Amico - Neuromuscular Disorders 2019 cited by 53
