Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR

Authors: Jasmina Cehajic‐Kapetanovic, Kanmin Xue, Cristina Martínez-Fernández de la Cámara, Anika Nanda, Alexandra Davies, Laura J. Taylor, Anna Paola Salvetti, M. Dominik Fischer, James Aylward, Alun R. Barnard, Jasleen K. Jolly, Edmond Luo, Brandon J. Lujan, Tuyen Ong, Aniz Girach, Graeme C. Black, Ninel Z. Gregori, Janet L. Davis, Potyra R. Rosa, Andrew Lotery, Byron L. Lam, Paulo Stanga, Robert E. MacLaren - Nature Medicine 2020 cited by 363