Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease

Authors: Bryan Zeitler, Steven Froelich, Kimberly Marlen, David A. Shivak, Qi Yu, Davis Li, Jocelynn R. Pearl, Jeffrey C. Miller, Lei Zhang, David E. Paschon, Sarah J. Hinkley, Irina Ankoudinova, Stephen C.-T. Lam, Dmitry Guschin, Lexi Kopan, Jennifer M. Cherone, Hoang-Oanh B. Nguyen, Guijuan Qiao, Yasaman Ataei, Matthew Mendel, Rainier Amora, Richard Surosky, Josée Laganière, B. Joseph Vu, Anand Narayanan, Yalda Sedaghat, Karsten Tillack, Christina Thiede, Annette Gärtner, Seung Kwak, Jonathan Bard, Ladislav Mrzljak, Larry Park, Taneli Heikkinen, Kimmo Lehtimäki, Marie Svedberg, Jenny Häggkvist, Lenke Tari, Miklós Tóth, Andrea Varrone, Christer Halldin, Andrea E. Kudwa, Sylvie Ramboz, Michelle Day, Jyothisri Kondapalli, D. James Surmeier, Fyodor D. Urnov, Philip D. Gregory, Edward J. Rebar, Ignacio Muñoz-Sanjuán, H. Steve Zhang - Nature Medicine 2019 cited by 220