SMN2 splice modulators enhance U1–pre-mRNA association and rescue SMA mice

Authors: James Palacino, Susanne E. Swalley, Cheng Song, Atwood K. Cheung, Lei Shu, Xiaolu Zhang, Mailin Van Hoosear, Youngah Shin, Donovan N. Chin, Caroline Gubser Keller, Martin Beibel, Nicole Renaud, Thomas M. Smith, Michael Salcius, Xiaoying Shi, Marc Hild, Rebecca Servais, Monish Jain, Lin Deng, Caroline Bullock, Michael D. McLellan, Sven Schuierer, Leo Murphy, Marcel J. J. Blommers, Cecile Blaustein, Frada Berenshteyn, Arnaud Lacoste, Jason R. Thomas, Guglielmo Roma, Gregory A. Michaud, Brian S. Tseng, Jeffery A. Porter, Vic E. Myer, John A. Tallarico, Lawrence G. Hamann, Daniel Curtis, Mark C. Fishman, William F. Dietrich, Natalie A. Dales, Rajeev Sivasankaran - Nature Chemical Biology 2015 cited by 428