Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study

Authors: David Adams, Michael Polydefkis, Alejandra González‐Duarte, Jonas Wixner, Arnt V. Kristen, Hartmut Schmidt, John L. Berk, Inés Asunción Losada López, Angela Dispenzieri, Dianna Quan, Isabel Conceição, Michel Slama, Julian D. Gillmore, Theodoros Kyriakides, Senda Ajroud‐Driss, Márcia Waddington‐Cruz, Michelle M. Mezei, Violaine Planté‐Bordeneuve, Shahram Attarian, Elizabeth A. Mauricio, Thomas H. Brannagan, Mitsuharu Ueda, Emre Aldinc, Jing Jing Wang, Matthew T. White, John Vest, Erhan Berber, Marianne T. Sweetser, Teresa Coelho, Giuseppe Vita, Vincenzo Rizzo, Massimo Russo, Anna Mazzeo, Luca Gentile, John L. Berk, Caitlin Brueckner, Victoria Lazzari, Janice F. Wiesman, Douglas DeLong, Jennifer Victory, James A. R. Dalton, John J. May, Catherine Gilmore, Shahram Attarian, Saran Diallo, Émilien Delmont, Jean Pouget, Annie Verschueren, Aude‐Marie Grapperon, Emmanuelle Salort‐Campana, Isabel Conceição, Ana Tarina Alvarez Lopes, Filipa Lamas, Carlos Marques‐Neves, José Castro, Pedro Pereira, Isabel Castro, Ana Franco, Miguel Oliveira Santos, Conceição de Azevedo Coutinho, Catarina Falcão de Campos, Teresa Coelho, Antonio Hipólito Reis, Nuno Correia, Javier Martínez Pérez, Ana Silva, Cristina Alves, Márcio Cardoso, Kátia Valdrez, Julia R Monte, Bernardete Pessoa, Nádia Guimarães, Mónica Freitas, Joana Ramalho, Natália Ferreira, Daisuke Kuzume, Céline Tard, Nawal Waucquier, Isabelle Rougeaux, Sylvie Brice, Emmanuelle Kasprzyk, Elise Elrezzi, Sayah Meguig, É. Hachulla, Clément Gauvain, Maria-Claire Migaud-Chervy, Dominique Deplanque, Elsa Jozefowicz, Loïc Lebellec, David B. Adams, Line Balaya-Gouraya, Nathalie Jehan Lacour, Halima Bournane, Nathalie Martin, Mongia Elabed, Niamey Sacko, Yasmine Boubrit, Amina Gaouar, Fetra Rakotondratafika, Marie Théaudin-Saliou, Cécile Cauquil-Michon, Céline Labeyrie, Adeline Not, Abdallah Al‐Salameh, Anne-Lise Lecoq, Maeva Stephant, Andoni Echaniz‐Laguna, Laurent Becquemont, Guillemette Beaudonnet, Vincent Algalarrondo, Ludivine Eliahou, Michel Slama, Antoine Rousseau, Aïssatou Signaté, Emeline Berthelot, Jocelyn Inamo, Violaine Planté‐Bordeneuve, Laetitia Vervoitte, Cécile Focseneanu, Thierry Gendre, Raphaele Arrouasse, Samar S. Ayache, Laura Ernande, Philippe Le Corvoisier, Hayet Salhi, Ariane Choumert, Vincent Ehinger, J. Pérez Ruiz, Cyril Charlin, Thomas Megelin, Thomas H. Brannagan, Raisy Fayerman, Arreum Kim, Allan Paras, Leidy González, Steven Tsang, Fernanda Wajnsztajn, Jeffrey Shije, Christina Ulane, Inna Kleyman, Louis H. 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Michael Martinez, Cristina Descals, Mercedes Usón, Francisco Jose Vega, Antoni Figuerola, Carles Montalà, Márcia Waddington‐Cruz, Moises Dias da Silva, Renata Gervais de Santa Rosa, Luiz Felipe Pinto, Marcus Vinícius Pinto, Amanda Cardoso Berensztejn, Fábio Barroso, Andrea Lautre, Lucas Orellana, Maria Alejandra González-Duarte Briseño, Karla Cárdenas‐Soto, Brenda Poled Jiménez López, Sandra Lorena Pérez-Castañeda, Carlos Cantú‐Brito, David Rivera de la Parra, Jose Pablo Hernandez Reyes, Maria del Mar Saniger Alba, Elia Criollo Mora, Yeşim Parman, Kus Jülide Rezzan, Erdi Şahin, Nail Güven Serbest, Hacer Durmuş, Arman Çakar, Nuriye Ilknur Tugal Tutkun, Saçit Karamürsel, Ali Elitok, Nermin G Sirin Inan, Emre Altinkurt, Michael Polydefkis, Jing Ye, Adriane C Allen, Vinay Chaudhry, R. J. Jarrett, Neil M. Bressler, Kathleen Burks, Qingfeng Liu, Mohammad Khoshnoodi, Daniel P. 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