Safety and efficacy of ganaxolone in patients with CDKL5 deficiency disorder: results from the double-blind phase of a randomised, placebo-controlled, phase 3 trial

著者: Elia Pestana‐Knight, Sam Amin, Nadia Bahi‐Buisson, Tim A. Benke, J. Helen Cross, Scott Demarest, Heather E. Olson, Nicola Specchio, Thomas R. Fleming, Alex A. Aimetti, Maciej Ga̧sior, Orrin Devinsky, Marigold Trial Group - University College London 2022 被引用: 130