Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial

著者: Nicola G. Ghazi, Emad B. Abboud, Sawsan R. Nowilaty, Hisham Alkuraya, Abdulrahman Alhommadi, Huimin Cai, Rui Hou, Wen‐Tao Deng, Sanford L. Boye, Abdulrahman Almaghamsi, Fahad Al Saikhan, Hassan Al-Dhibi, David G. Birch, Christopher Chung, Dilek Çolak, Matthew M. LaVail, Douglas Vollrath, Kirsten Erger, Wen‐qiu Wang, Thomas J. Conlon, Kang Zhang, William W. Hauswirth, Fowzan S. Alkuraya - Human Genetics 2016 被引用: 240