Development of a gene-editing approach to restore vision loss in Leber congenital amaurosis type 10
著者: Morgan L. Maeder, Michael Stefanidakis, Christopher J. Wilson, Reshica Baral, Luis Barrera, George S. Bounoutas, David Bumcrot, Hoson Chao, Dawn Ciulla, Jennifer A. DaSilva, Abhishek Dass, Vidya Dhanapal, Tim Fennell, Ari E. Friedland, Georgia Giannoukos, Sebastian Gloskowski, Alexandra Glucksmann, Gregory Gotta, Hariharan Jayaram, Scott Haskett, Bei Hopkins, Joy E. Horng, Shivangi Joshi, Eugenio Marco, Rina J. Mepani, Deepak Reyon, Terence Ta, Diana Tabbaa, Steven J. Samuelsson, Shen Shen, Maxwell N. Skor, Pam Stetkiewicz, Tongyao Wang, Clifford Yudkoff, Vic E. Myer, Charles F. Albright, Haiyan Jiang - Nature Medicine 2019 被引用: 706
