Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study

著者: Thomas Klopstock, Fernando Tricta, Lynne Neumayr, Ivan Karin, Giovanna Zorzi, Caroline Fradette, Tomasz Kmieć, Boriana Büchner, Hannah E. Steele, Rita Horváth, Patrick F. Chinnery, Anna Basu, Clemens Küpper, Christiane Neuhofer, Bernadette Kálmán, Petr Dušek, Zühal Yapıcı, Ian Wilson, Feng Zhao, Federica Zibordi, Nardo Nardocci, Christine Aguilar, Susan J. Hayflick, Michael Spino, Andrew M. Blamire, Penelope Hogarth, Elliott Vichinsky - The Lancet 2019 被引用: 146