A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells

Authors: Courtney S. Young, Michael R. Hicks, Natalia Ermolova, Haruko Nakano, Majib Jan, Shahab Younesi, Saravanan Karumbayaram, Chino Kumagai-Cresse, Derek Wang, Jerome A. Zack, Donald B. Kohn, Atsushi Nakano, Stanley F. Nelson, M. Carrie Miceli, Melissa J. Spencer, April D. Pyle - Cell stem cell 2016 cited by 382