Donald B. Kohn
Active 1986–2025
- 162
- Papers
- 22,737
- Citations
- 91
- h-index
- 153
- i10-index
Citations
Citation sources
Countries
Institutions
Fields
- Biochemistry, Genetics and Molecular Biology51.8%
- Medicine28.6%
- Immunology and Microbiology14.6%
- Neuroscience1.7%
- Engineering1.6%
- Materials Science0.5%
- Other1.2%
Topics
- CRISPR and Genetic Engineering9.9%
- Virus-based gene therapy research9.9%
- CAR-T cell therapy research5.9%
- RNA Interference and Gene Delivery5.8%
- Immune Cell Function and Interaction3.1%
- Immunodeficiency and Autoimmune Disorders3%
- Other62.4%
Coauthors
- Roger P. Hollis27
- Neena Kapoor22
- Linda M. Griffith17
- Morton J. Cowan16
- Gay M. Crooks15
- Sung‐Yun Pai15
- Beatriz Campo-Fernández14
- Brent R. Logan14
- Rebecca H. Buckley14
- Theodore B. Moore14
- Xiaoyan Wang14
- Blachy J. Dávila Saldaña13
- Christopher C. Dvorak13
- Geoff D.E. Cuvelier13
- Jennifer Heimall12
- Jennifer M. Puck12
- Luigi D. Notarangelo11
- Shanmuganathan Chandrakasan11
- Deepak Chellapandian10
- Jan A. Nolta10
- Lauri M. Burroughs10
- Richard J. O’Reilly10
- Satiro De Oliveira10
- Sharat Chandra10
All papers
- Gene therapy comes of age
Authors: Cynthia E. Dunbar, Katherine A. High, J. Keith Joung, Donald B. Kohn, Keiya Ozawa, Michel Sadelain - Science 2018 cited by 1,378
- Generation of mature T cells from human hematopoietic stem and progenitor cells in artificial thymic organoids
Authors: Christopher S. Seet, Chongbin He, Michael T. Bethune, Suwen Li, Brent Chick, Eric H. Gschweng, Yuhua Zhu, Kenneth Kim, Donald B. Kohn, David Baltimore, Gay M. Crooks, Amélie Montel‐Hagen - Nature Methods 2017 cited by 268
- Successes and challenges in clinical gene therapy
Authors: Donald B. Kohn, Yvonne Y. Chen, Melissa J. Spencer - Gene Therapy 2023 cited by 159
- Generation of allogeneic CAR-NKT cells from hematopoietic stem and progenitor cells using a clinically guided culture method
Authors: Yan-Ruide Li, Yang Zhou, Jiaji Yu, Kwang Gi Kim, Miao Li, Derek Lee, Kuangyi Zhou, Yuning Chen, Yichen Zhu, Yu-Chen Wang, Zhe Li, Yanqi Yu, Zachary Spencer Dunn, Wenbin Guo, Xinjian Cen, Tiffany Husman, Aarushi Bajpai, Adam B. Kramer, Matthew Wilson, Ying Fang, Jie Huang, Shuo Li, Yonggang Zhou, Yuchong Zhang, Zoe Hahn, Enbo Zhu, Feiyang Ma, Calvin Pan, Aldons J. Lusis, Jin Zhou, Christopher S. Seet, Donald B. Kohn, Pin Wang, Xianghong Jasmine Zhou, Matteo Pellegrini, Benjamin Puliafito, Sarah Larson, Lili Yang - Nature Biotechnology 2024 cited by 95
- Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells
Authors: Mark A. DeWitt, Wendy Magis, Nicolas Bray, Tianjiao Wang, Jennifer R. Berman, Fabrizia Urbinati, Seok‐Jin Heo, Therese Mitros, Denise P. Muñoz, Dario Boffelli, Donald B. Kohn, Mark C. Walters, Dana Carroll, David I. K. Martin, Jacob E. Corn - Science Translational Medicine 2016 cited by 495
- Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
Authors: Donald B. Kohn, Claire Booth, Kit L. Shaw, Jinhua Xu‐Bayford, Elizabeth Garabedian, Valentina Trevisan, Denise A. Carbonaro-Sarracino, Kajal Soni, Dayna Terrazas, Katie Snell, Alan K. Ikeda, Diego León‐Rico, Theodore B. Moore, Karen Buckland, Ami J. Shah, Kimberly Gilmour, Satiro De Oliveira, Christine Rivat, Gay M. Crooks, Natalia Izotova, John Tse, Stuart Adams, Sally Shupien, Hilory Ricketts, Alejandra Davila, Chilenwa Uzowuru, Amalia Icreverzi, Provaboti Barman, Beatriz Campo Fernandez, Roger P. Hollis, Maritess Coronel, Allen Chi-Shing Yu, Krista Chun, Christian E. Casas, Ruixue Zhang, Serena Arduini, Frances Lynn, Mahesh Kudari, Andrea Spezzi, Marco Zahn, Rene Heimke, Ivan Labik, Roberta Parrott, Rebecca H. Buckley, Lilith Reeves, Kenneth Cornetta, Robert Sokolic, Michael S. Hershfield, Manfred Schmidt, Fabio Candotti, Harry L. Malech, Adrian J. Thrasher, H. Bobby Gaspar - New England Journal of Medicine 2021 cited by 218
- Human T cell generation is restored in CD3δ severe combined immunodeficiency through adenine base editing
Authors: Grace E. McAuley, Gloria Yiu, Patrick Chang, Gregory A. Newby, Beatriz Campo-Fernández, Sorel Fitz‐Gibbon, Wu Xiaomeng, Sung‐Hae Kang, Amber Garibay, Jeffrey Butler, Valentina Christian, Ryan L. Wong, Kelcee A. Everette, Anthony Azzun, Hila Gelfer, Christopher S. Seet, Aru Narendran, Luis Murguía-Favela, Zulema Romero, Nicola Wright, David R. Liu, Gay M. Crooks, Donald B. Kohn - Cell 2023 cited by 82
- Development of allogeneic HSC-engineered iNKT cells for off-the-shelf cancer immunotherapy
Authors: Yan-Ruide Li, Yang Zhou, Kwang Gi Kim, Yanni Zhu, Feiyang Ma, Jiaji Yu, Yu-Chen Wang, Xianhui Chen, Zhe Li, Samuel Zeng, Xi Wang, Derek Lee, Josh Ku, Tasha Tsao, Christian Hardoy, Jie Huang, Donghui Cheng, Amélie Montel‐Hagen, Christopher S. Seet, Gay M. Crooks, Sarah Larson, Joshua Sasine, Xiaoyan Wang, Matteo Pellegrini, Antoni Ribas, Donald B. Kohn, Owen N. Witte, Pin Wang, Lili Yang - Cell Reports Medicine 2021 cited by 104
- Transplantation Outcomes for Severe Combined Immunodeficiency, 2000–2009
Authors: Sung‐Yun Pai, Brent R. Logan, Linda M. Griffith, Rebecca H. Buckley, Roberta Parrott, Christopher C. Dvorak, Neena Kapoor, I. Celine Hanson, Alexandra H. Filipovich, Soma Jyonouchi, Kathleen E. Sullivan, Trudy N. Small, Lauri M. Burroughs, Suzanne Skoda‐Smith, Ann E. Haight, Audrey Grizzle, Michael A. Pulsipher, Ka Wah Chan, Ramsay Fuleihan, Élie Haddad, Brett Loechelt, Victor M. Aquino, Alfred P. Gillio, Jeffrey Davis, Alan P. Knutsen, Angela R. Smith, Theodore B. Moore, Marlis L. Schroeder, Frederick D. Goldman, James A. Connelly, Matthew H. Porteus, Qun Xiang, William T. Shearer, Thomas A. Fleisher, Donald B. Kohn, Jennifer M. Puck, Luigi D. Notarangelo, Morton J. Cowan, Richard J. O’Reilly - New England Journal of Medicine 2014 cited by 771
- Lentiviral gene therapy for X-linked chronic granulomatous disease
Authors: Donald B. Kohn, Claire Booth, Elizabeth M. Kang, Sung‐Yun Pai, Kit L. Shaw, Giorgia Santilli, Myriam Armant, Karen Buckland, Uimook Choi, Suk See De Ravin, Morna J. Dorsey, Caroline Y. Kuo, Diego León‐Rico, Christine Rivat, Natalia Izotova, Kimberly Gilmour, Katie Snell, Jinhua Xu-Bayford Dip, Jinan Darwish, Emma Morris, Dayna Terrazas, Leo D. Wang, Christopher Bauser, Tobias Paprotka, Douglas B. Kuhns, John Gregg, Hayley E. Raymond, J.K. Everett, Géraldine Honnet, Luca Biasco, Peter E. Newburger, Frederic D. Bushman, Manuel Grez, H. Bobby Gaspar, David A. Williams, Harry L. Malech, Anne Galy, Adrian J. Thrasher - Nature Medicine 2020 cited by 253
- Analyzing CRISPR genome-editing experiments with CRISPResso
Authors: Luca Pinello, Matthew C. Canver, Megan D. Hoban, Stuart H. Orkin, Donald B. Kohn, Daniel E. Bauer, Guo‐Cheng Yuan - Nature Biotechnology 2016 cited by 498
- The diagnosis of severe combined immunodeficiency (SCID): The Primary Immune Deficiency Treatment Consortium (PIDTC) 2022 Definitions
Authors: Christopher C. Dvorak, Élie Haddad, Jennifer Heimall, Elizabeth Dunn, Rebecca H. Buckley, Donald B. Kohn, Morton J. Cowan, Sung‐Yun Pai, Linda M. Griffith, Geoff D.E. Cuvelier, Hesham Eissa, Ami J. Shah, Richard J. O’Reilly, Michael A. Pulsipher, Nicola Wright, Roshini S. Abraham, Lisa Forbes Satter, Luigi D. Notarangelo, Jennifer M. Puck - Journal of Allergy and Clinical Immunology 2022 cited by 125
- Newborn Screening for Severe Combined Immunodeficiency in 11 Screening Programs in the United States
Authors: Antonia Kwan, Roshini S. Abraham, Robert J. Currier, Amy Brower, Karen Andruszewski, Jordan K. Abbott, Mei Baker, Mark Ballow, Louis Bartoshesky, Francisco A. Bonilla, Charles D. Brokopp, Edward G. Brooks, Michele Caggana, Jocelyn Celestin, Joseph A. Church, Anne Marie Comeau, James A. Connelly, Morton J. Cowan, Charlotte Cunningham‐Rundles, Trivikram Dasu, Nina Dave, M. Teresa de la Morena, Ulrich Duffner, Chin-To Fong, Lisa R. Forbes, Debra Freedenberg, Erwin W. Gelfand, Jaime E. Hale, I. Celine Hanson, Beverly N. Hay, Diana Hu, Anthony J. Infante, Daisy Johnson, Neena Kapoor, Denise M. Kay, Donald B. Kohn, Rachel Lee, Heather K. Lehman, Zhili Lin, Fred Lorey, Aly Abdel‐Mageed, Adrienne Manning, Sean McGhee, Theodore B. Moore, Stanley J. Naides, Luigi D. Notarangelo, Jordan S. Orange, Sung‐Yun Pai, Matthew H. Porteus, Ray Rodríguez, Neil Romberg, John M. Routes, Mary Ruehle, Arye Rubenstein, Carlos A. Saavedra‐Matiz, G. E. M. Scott, Patricia M. Scott, Elizabeth Secord, Christine M. Seroogy, William T. Shearer, Subhadra Siegel, Stacy K. Silvers, E. Richard Stiehm, Robert W. Sugerman, John L. Sullivan, Susan Tanksley, Millard L. Tierce, James Verbsky, Beth Vogel, Rosalyn Walker, Kelly Walkovich, Jolán E. Walter, Richard L. Wasserman, Michael S. Watson, Geoffrey A. Weinberg, Leonard B. Weiner, Heather Wood, Anne Yates, Jennifer M. Puck - JAMA 2014 cited by 673
- Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium
Authors: Monica S. Thakar, Brent R. Logan, Jennifer M. Puck, Elizabeth Dunn, Rebecca H. Buckley, Morton J. Cowan, Richard J. O’Reilly, Neena Kapoor, Lisa Forbes Satter, Sung‐Yun Pai, Jennifer Heimall, Sharat Chandra, Christen L. Ebens, Deepak Chellapandian, Olatundun Williams, Lauri M. Burroughs, Blachy J. Dávila Saldaña, Ahmad Rayes, Lisa Madden, Shanmuganathan Chandrakasan, Jeffrey J. Bednarski, Kenneth B. DeSantes, Geoff D.E. Cuvelier, Pierre Teira, Alfred P. Gillio, Hesham Eissa, Alan P. Knutsen, Frederick D. Goldman, Victor M. Aquino, Evan Shereck, Theodore B. Moore, Emi Caywood, Mark T. Vander Lugt, Jacob Rozmus, Larisa Broglie, Lolie C. Yu, Ami J. Shah, Jeffrey R. Andolina, Xuerong Liu, Roberta Parrott, Jasmeen Dara, Susan E. Prockop, Caridad Martinez, Malika Kapadia, Soma Jyonouchi, Kathleen E. Sullivan, Jack Bleesing, Sonali Chaudhury, Aleksandra Petrović, Michael D. Keller, Troy C. Quigg, Suhag Parikh, Shalini Shenoy, Christine M. Seroogy, Tamar Rubin, Hélène Decaluwe, John M. Routes, Troy R. Torgerson, Jennifer W. Leiding, Michael A. Pulsipher, Donald B. Kohn, Linda M. Griffith, Élie Haddad, Christopher C. Dvorak, Luigi D. Notarangelo - The Lancet 2023 cited by 113
- Development of Hematopoietic Stem Cell-Engineered Invariant Natural Killer T Cell Therapy for Cancer
Authors: Yanni Zhu, Drake J. Smith, Yang Zhou, Yan-Ruide Li, Jiaji Yu, Derek Lee, Yu-Chen Wang, Stefano Di Biase, Xi Wang, Christian Hardoy, Josh Ku, Tasha Tsao, Levina J. Lin, Alexander Pham, Heesung Moon, Jami McLaughlin, Donghui Cheng, Roger P. Hollis, Beatriz Campo-Fernández, Fabrizia Urbinati, Wei Liu, Larry Pang, Valerie Rezek, Beata Berent-Maoz, Mignonette H. Macabali, David W. Gjertson, Xiaoyan Wang, Zoran Galić, Scott G. Kitchen, Dong Sung An, Siwen Hu‐Lieskovan, Paula Kaplan‐Lefko, Satiro De Oliveira, Christopher S. Seet, Sarah Larson, Stephen J. Forman, James R. Heath, Jerome A. Zack, Gay M. Crooks, Caius G. Radu, Antoni Ribas, Donald B. Kohn, Owen N. Witte, Lili Yang - Cell stem cell 2019 cited by 97
- Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned
Authors: Richard A. Morgan, David Gray, Anastasia Lomova, Donald B. Kohn - Cell stem cell 2017 cited by 244
- Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates
Authors: Zulema Romero, Anastasia Lomova, Suzanne Saïd, Alexandra Miggelbrink, Caroline Y. Kuo, Beatriz Campo-Fernández, Megan D. Hoban, Katelyn E. Masiuk, Danielle N. Clark, Joseph Long, Julie M. Sanchez, Miriam Velez, Eric Miyahira, Ruixue Zhang, Devin Brown, Xiaoyan Wang, Yerbol Z. Kurmangaliyev, Roger P. Hollis, Donald B. Kohn - Molecular Therapy 2019 cited by 126
- Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells
Authors: Megan D. Hoban, Gregory J. Cost, Matthew Mendel, Zulema Romero, Michael L. Kaufman, Alok V. Joglekar, Michelle Ho, Dianne Lumaquin, David Gray, Georgia R. Lill, Aaron Cooper, Fabrizia Urbinati, Shantha Senadheera, Allen Zhu, Peiqi Liu, David E. Paschon, Lei Zhang, Edward J. Rebar, Andrew Wilber, Xiaoyan Wang, Philip D. Gregory, Michael C. Holmes, Andreas Reik, Roger P. Hollis, Donald B. Kohn - Blood 2015 cited by 320
- Newborn Screening for Severe Combined Immunodeficiency and T-cell Lymphopenia in California, 2010–2017
Authors: George S. Amatuni, Robert J. Currier, Joseph A. Church, Tracey Bishop, Elena Grimbacher, Alan A. Nguyen, Rajni Agarwal‐Hashmi, Constantino P. Aznar, Manish J. Butte, Morton J. Cowan, Morna J. Dorsey, Christopher C. Dvorak, Neena Kapoor, Donald B. Kohn, M. Louise Markert, Theodore B. Moore, Stanley J. Naides, Stanley Sciortino, Lisa Feuchtbaum, Rasoul A. Koupaei, Jennifer M. Puck - PEDIATRICS 2019 cited by 197
- A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency
Authors: Salima Hacein‐Bey‐Abina, Sung‐Yun Pai, H. Bobby Gaspar, Myriam Armant, Charles C. Berry, Stéphane Blanche, Jack Bleesing, Johanna Blondeau, Helen de Boer, Karen Buckland, Laure Caccavelli, Guilhem Cros, Satiro De Oliveira, Karen S. Fernández, Dongjing Guo, Chad E. Harris, Gregory Hopkins, Leslie Lehmann, Annick Lim, Wendy B. London, Johannes C.M. van der Loo, Nirav Malani, Frances Male, Punam Malik, María Angélica Marinovic, Anne-Marie McNicol, Despina Moshous, Bénédicte Neven, Matías Oleastro, Capucine Pïcard, Jerome Ritz, Christine Rivat, Axel Schambach, Kit L. Shaw, Eric A. Sherman, Leslie E. Silberstein, Emmanuelle Six, Fabien Touzot, Alla V. Tsytsykova, Jinhua Xu‐Bayford, Christopher Baum, Frederic D. Bushman, Alain Fischer, Donald B. Kohn, Alexandra H. Filipovich, Luigi D. Notarangelo, Marina Cavazzana, David A. Williams, Adrian J. Thrasher - New England Journal of Medicine 2014 cited by 410
- Immune reconstitution and survival of 100 SCID patients post–hematopoietic cell transplant: a PIDTC natural history study
Authors: Jennifer Heimall, Brent R. Logan, Morton J. Cowan, Luigi D. Notarangelo, Linda M. Griffith, Jennifer M. Puck, Donald B. Kohn, Michael A. Pulsipher, Suhag Parikh, Caridad Martinez, Neena Kapoor, Richard J. O’Reilly, Michael Boyer, Sung‐Yun Pai, Frederick D. Goldman, Lauri Burroughs, Sharat Chandra, Morris Kletzel, Monica S. Thakar, James A. Connelly, Geoff D.E. Cuvelier, Blachy J. Dávila Saldaña, Evan Shereck, Alan P. Knutsen, Kathleen E. Sullivan, Kenneth B. DeSantes, Alfred P. Gillio, Élie Haddad, Aleksandra Petrović, Troy C. Quigg, Angela R. Smith, Elizabeth Stenger, Ziyan Yin, William T. Shearer, Thomas A. Fleisher, Rebecca H. Buckley, Christopher C. Dvorak - Blood 2017 cited by 266
- Adoptive Transfer of MART-1 T-Cell Receptor Transgenic Lymphocytes and Dendritic Cell Vaccination in Patients with Metastatic Melanoma
Authors: Thinle Chodon, Begoña Comı́n-Anduix, Bartosz Chmielowski, Richard C. Koya, Zhongqi Wu, Martin Auerbach, Charles Ng, Earl Avramis, Elizabeth Seja, Arturo Villanueva, Tara A. McCannel, Akira Ishiyama, Johannes Czernin, Caius G. Radu, Xiaoyan Wang, David W. Gjertson, Alistair J. Cochran, Kenneth Cornetta, Deborah Jean Lee Wong, Paula Kaplan‐Lefko, Omid Hamid, Wolfram E. Samlowski, Peter A. Cohen, Gregory A. Daniels, Bijay Mukherji, Lili Yang, Jerome A. Zack, Donald B. Kohn, James R. Heath, John A. Glaspy, Owen N. Witte, David Baltimore, James S. Economou, Antoni Ribas - Clinical Cancer Research 2014 cited by 253
- Gene Therapies for Primary Immune Deficiencies
Authors: Lisa A. Kohn, Donald B. Kohn - Frontiers in Immunology 2021 cited by 69
- A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells
Authors: Courtney S. Young, Michael R. Hicks, Natalia Ermolova, Haruko Nakano, Majib Jan, Shahab Younesi, Saravanan Karumbayaram, Chino Kumagai-Cresse, Derek Wang, Jerome A. Zack, Donald B. Kohn, Atsushi Nakano, Stanley F. Nelson, M. Carrie Miceli, Melissa J. Spencer, April D. Pyle - Cell stem cell 2016 cited by 382
